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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
47
Publications avec texte intégral
Open Access
73 %
Mots clés
Cells
Cell Biology
Human Umbilical Vein Endothelial Cells
Modificateurs de gènes
Immunoglobulin Fc Fragments/pharmacology
Dystrophie Musculaire de Duchenne DMD
NNOS
DMD
Homeostasis
Multiresolution modeling
Gene expression
Knockout
Autophagy
Diseases
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Cultured
NAD+
Hepatocellular carcinoma
DHPR α1S
Gene Expression Regulation/drug effects
Activin Receptors
Génomique
Dynamin 2
Muscular Atrophy
Ex-vivo
Muscles/physiopathology
Myogenesis
Multi resolution modeling
LncRNA
CaV subunits
Calcium Channels
Morphogenesis
Liver
Antisense oligonucleotides
LncARN
Drp1
Delivery
Mdx mouse
Gene modifiers
Myotendinous junction
Animal/physiopathology
CaVβs
Epigenetics
Dystrophie musculaire de Becker
DMO
Molecular docking
Cell Line
Allele‐specific silencing therapy
Muscle development
Duchenne muscular dystrophy DMD
Dystrophin central domain
Energy Metabolism/drug effects
MiARN
Cell homeostasis
Cardiomyopathie
Long QT
Dystrophine
Multi exon skipping
Invivo
L-Type
Dystrophy
Clinical trials
LKB1
Male
Dystrophin
Long noncoding RNA
Becker muscular dystrophy BMD
Dystrophie Musculaire de Becker BMD
Becker BMD muscular dystrophy
CTNNB1
Inbred mdx
Base Sequence
Duchenne muscular dystrophy
Hear
Muscle Strength
Genomic
Calcium
Dystrophin-EGFP
Skeletal muscle
Inbred C57BL
Muscle Biology
Molecular Sequence Data
Metabolism
Animals
Becker muscular dystrophy
Cardiomyopathy
Mitochondrial fission
MES
Exon skipping
Inhibitors
Humans
BMD
Centronuclear myopathy
Cachexia
CD38
Muscular Dystrophy
Duchenne DMD dystrophy
Mice
Muscular dystrophy
Muscle