index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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Cells Cell Biology Human Umbilical Vein Endothelial Cells Modificateurs de gènes Immunoglobulin Fc Fragments/pharmacology Dystrophie Musculaire de Duchenne DMD NNOS DMD Homeostasis Multiresolution modeling Gene expression Knockout Autophagy Diseases Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Cultured NAD+ Hepatocellular carcinoma DHPR α1S Gene Expression Regulation/drug effects Activin Receptors Génomique Dynamin 2 Muscular Atrophy Ex-vivo Muscles/physiopathology Myogenesis Multi resolution modeling LncRNA CaV subunits Calcium Channels Morphogenesis Liver Antisense oligonucleotides LncARN Drp1 Delivery Mdx mouse Gene modifiers Myotendinous junction Animal/physiopathology CaVβs Epigenetics Dystrophie musculaire de Becker DMO Molecular docking Cell Line Allele‐specific silencing therapy Muscle development Duchenne muscular dystrophy DMD Dystrophin central domain Energy Metabolism/drug effects MiARN Cell homeostasis Cardiomyopathie Long QT Dystrophine Multi exon skipping Invivo L-Type Dystrophy Clinical trials LKB1 Male Dystrophin Long noncoding RNA Becker muscular dystrophy BMD Dystrophie Musculaire de Becker BMD Becker BMD muscular dystrophy CTNNB1 Inbred mdx Base Sequence Duchenne muscular dystrophy Hear Muscle Strength Genomic Calcium Dystrophin-EGFP Skeletal muscle Inbred C57BL Muscle Biology Molecular Sequence Data Metabolism Animals Becker muscular dystrophy Cardiomyopathy Mitochondrial fission MES Exon skipping Inhibitors Humans BMD Centronuclear myopathy Cachexia CD38 Muscular Dystrophy Duchenne DMD dystrophy Mice Muscular dystrophy Muscle